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Duchenne Muscular Dystrophy — Gene Therapy & Clinical Trials | FollowGene
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Duchenne Muscular Dystrophy
Duchenne Muscular Dystrophy
Prevalence:
~300K
neuromuscular
Official
·
OMIM:310200
Official
·
ORPHA98896
X-linked inherited disease characterized by progressive muscle weakness.
Associated Genes
DMD
Dystrophin
Chromosome X
X-Linked Recessive