Latest articles about gene therapy and genetic diseases.
Current list of gene therapies approved by the FDA and EMA: which disease, which gene, which technology, and the official approval number. Every row links to the regulatory record.
What a clinical trial is, what the phases mean, how to read eligibility criteria, and how to approach a gene therapy trial step by step — a practical guide based on ClinicalTrials.gov records.
Casgevy (exagamglogene autotemcel) was the first CRISPR-Cas9 therapy ever approved. Why does it target BCL11A, how does fetal haemoglobin come back, and what does the treatment involve?
GuideHow does CRISPR-Cas9 work, which diseases is it used for, and what are its limitations?
ResearchLatest developments in GJB2 and OTOF genes, clinical trials, and treatment prospects.
TransparencyWhich databases does FollowGene use? How does the reliability badge system work?