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Hemophilia B — Gene Therapy & Clinical Trials | FollowGene
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The information on this page is for informational purposes only and does not constitute medical advice. Consult your genetic counselor or specialist physician for treatment decisions.
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Hemophilia B
Hemophilia B
Prevalence:
~30K
hematologic
Official
·
OMIM:306900
Official
·
ORPHA101
Inherited bleeding disorder due to factor IX deficiency.
Approved Therapies
Hemgenix (etranacogene dezaparvovec)
FDA Approved
11/22/2022
AAV Gene Therapy
Associated Genes
F9
Coagulation Factor IX
Chromosome X
X-Linked Recessive