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Stargardt Disease — Gene Therapy & Clinical Trials | FollowGene
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Stargardt Disease
Stargardt Disease
Prevalence:
1/10000
ophthalmologic
Official
·
OMIM:248200
Official
·
ORPHA827
Juvenile macular degeneration due to ABCA4 gene mutations.
Associated Genes
ABCA4
ATP Binding Cassette Subfamily A Member 4
Chromosome 1
Autosomal Recessive