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WAS

—WASP Actin Nucleation Promoting Factor

Chromosome: X

Location: X:48676593-48691431

OMIM: 300392

Ensembl: ENSG00000015285

Official·OMIM:300392 Official·ENSG00000015285

Encodes WASP protein. Mutations cause Wiskott-Aldrich syndrome.

Treatment Roadmap — WAS

Preclinical

Phase 1

58 trial

Phase 2

135 trial

Phase 3

68 trial

Approved

Clinical trials have approximately 10% success rate. This roadmap shows the current status, not guaranteed outcomes.

Associated Diseases

Wiskott-Aldrich Syndrome

X-Linked RecessivePrevalence: 1/250000immunologic

Official·OMIM:301000 Official·ORPHA906

Summary

546

Clinical Trial

Approved Therapy

Registered Variant