This study investigates a gene therapy for Tay-Sachs disease. Anyone diagnosed with a hexosaminidase deficiency disease could be included. The study was carried out as a non-phase study and has been completed.
The summary above is a plain-language rendering of the official record. The original English title is shown for reference.
Criteria are reproduced from the ClinicalTrials.gov record in the original English. Only the trial team can determine eligibility.
Inclusion Criteria: Any person who has been diagnosed with a hexosaminidase deficiency disease can be included in this study. Exclusion Criteria: The only exclusion criteria is a desire not to participate in this study.