Gene Therapy for Tay-Sachs Disease

Plain-language summary

This study investigates a gene therapy for Tay-Sachs disease. Anyone diagnosed with a hexosaminidase deficiency disease could be included. The study was carried out as a non-phase study and has been completed.

The summary above is a plain-language rendering of the official record. The original English title is shown for reference.

Trial details

Phase

N/A

Status

Completed

Sponsor

University of Minnesota

Start date

12/1/2010

Estimated completion

8/1/2014

Countries

United States

Related genes

Locations

• Tampa, United States
• Minneapolis, United States

Eligibility criteria

Criteria are reproduced from the ClinicalTrials.gov record in the original English. Only the trial team can determine eligibility.

Inclusion Criteria:

Any person who has been diagnosed with a hexosaminidase deficiency disease can be included in this study.

Exclusion Criteria:

The only exclusion criteria is a desire not to participate in this study.