This study explores decision-making and quality of life among patients (and their families) who are eligible for gene therapy to treat a blood (hematologic) disease. Adults aged 18 and over eligible for gene therapy, or parents of eligible pediatric patients, may take part. It is a non-phase study that is enrolling by invitation.
The summary above is a plain-language rendering of the official record. The original English title is shown for reference.
Criteria are reproduced from the ClinicalTrials.gov record in the original English. Only the trial team can determine eligibility.
Inclusion Criteria: * adult patients (ages 18+) or parents of pediatric patients (\<age 18) eligible to receive treatment for their disease with gene therapy Exclusion Criteria: * Non-English-speaking